CRISPR for Neuromuscular Disorders: Gene Editing and Beyond

Volume: 34, Issue: 5, Pages: 341 - 353
Published: Sep 1, 2019
Abstract
This is a review describing advances in CRISPR/Cas-mediated therapies for neuromuscular disorders (NMDs). We explore both CRISPR-mediated editing and dead Cas approaches as potential therapeutic strategies for multiple NMDs. Last, therapeutic considerations, including delivery and off-target effects, are also...
Paper Details
Title
CRISPR for Neuromuscular Disorders: Gene Editing and Beyond
Published Date
Sep 1, 2019
Journal
Volume
34
Issue
5
Pages
341 - 353
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